Unmet needs for severe hemophilia A cases without inhibitors in Argentina: a cross-sectional study.

Abstract

Introduction. Hemophilia A (HA) is a rare inherited disorder due to a gene mutation encoding the clotting factor VIII. For Argentina, a prevalence of 10.4 per 100,000 males was reported in 2021. Through real-world data, we aim to describe the sociodemographic and clinical characteristics, outcomes and healthcare resources utilization of Argentinian HA individuals without inhibitors.