Rare pulmonary disease and orphan drugs: a path to the future

Abstract

The interest in rare diseases is growing. The progress in this field has been made possible by a coordinated action between respiratory researchers, health authorities and patients associations.

Some take-home messages from the 9th International Meeting on Pulmonary Rare Diseases and Orphan Drugs

“…Dissemination of updated knowledge on rare and ultra-rare respiratory diseases has always been a priority of the European Respiratory Review (ERR) [1,2]. In this issue, we publish the first of a collection of four articles that discuss hot topics with direct practical clinical consequences.…”